A Study to Evaluate SAGE-217 in Participants With Essential Tremor

Purpose

This study is a three-part, multicenter, Phase 2a study to evaluate the efficacy, safety, tolerability, and pharmacokinetics of SAGE-217 in adult participants with essential tremor.

Condition

  • Essential Tremor

Eligibility

Eligible Ages
Between 18 Years and 80 Years
Eligible Sex
All
Accepts Healthy Volunteers
No

Inclusion Criteria

  • Participant must have a diagnosis of Essential Tremor (ET), defined as bilateral postural tremor and kinetic tremor, involving hands and forearms, that is visible and persistent and the duration is >5 years prior to screening.

Exclusion Criteria

  • Participant has presence of abnormal neurological signs other than tremor or Froment's sign. - Participant has presence of known causes of enhanced physiological tremor. - Participant has concurrent or recent exposure (14 days prior to admission visit) to tremorogenic drugs. - Participant has had direct or indirect trauma to the nervous system within 3 months before the onset of tremor. - Participant has historical or clinical evidence of tremor with psychogenic origin. - Participant has convincing evidence of sudden tremor onset or evidence of stepwise deterioration of tremor.

Study Design

Phase
Phase 2
Study Type
Interventional
Allocation
Randomized
Intervention Model
Parallel Assignment
Primary Purpose
Treatment
Masking
Quadruple (Participant, Care Provider, Investigator, Outcomes Assessor)

Arm Groups

ArmDescriptionAssigned Intervention
Experimental
Part A: SAGE-217 Oral Solution
Participants received SAGE-217 10 mg oral solution on Day 1, 20 mg on Day 2 and 30 mg on Days 3 to 7 with food in the morning.
  • Drug: SAGE-217
    SAGE-217 Oral Solution
Experimental
Part A: SAGE-217 Capsules
Participants received SAGE-217 10 mg capsules on Day 1, 20 mg on Day 2 and 30 mg on Days 3 to 7, orally, with food in the morning.
  • Drug: SAGE-217
    SAGE-217 Capsules
Placebo Comparator
Part B: Placebo
Participants who received maximum tolerated dose of SAGE-217 in Part A and achieved response on Day 8 were randomized to receive to SAGE-217 matching placebo for 7 days beginning on Day 8 with food in the morning.
  • Drug: Placebo
    SAGE-217 matching placebo capsules
Experimental
Part B: SAGE-217 Capsules
Participants who received maximum tolerated dose of SAGE-217 in Part A and achieved response on Day 8 were randomized to receive to SAGE-217 for 7 days beginning on Day 8 with food in the morning.
  • Drug: SAGE-217
    SAGE-217 Capsules
Experimental
Part C: SAGE-217 Capsules
Participants received SAGE-217 10 mg capsules on Day 1, 20 mg on Day 2, 30 mg on Day 3, orally, with food in the evening. Beginning on Day 4 through Day 14, participants received a 40-mg total daily dose (administered as 10 mg with food in the morning and 30 mg with food in the evening).
  • Drug: SAGE-217
    SAGE-217 Capsules

More Details

Status
Completed
Sponsor
Biogen

Study Contact

Detailed Description

Part A of the study was an open-label design with morning dosing of SAGE-217 for 7 days and included 16 participants, 8 of whom qualified for, and entered, Part B. Part B had a double-blind, placebo-controlled, randomized withdrawal design with morning dosing for 7 days. Part C was an open-label design with morning and evening dosing for 14 days and included a different set of 18 participants. Parts A and B were stopped early (in advance of the planned sample size). This study was previously posted by Sage Therapeutics. In November 2023, sponsorship of the trial was transferred to Biogen.